Therapeutic target discovery

Low success rates in clinical trials remain a major challenge in drug development. We leverage our expertise and bring human genetic evidence to therapeutic target discovery and validation. We envision nominating therapeutic targets for disease subtypes based on their underlying biology.

  • Experiments by nature
  • Rare variant associations
  • Translational genomics and pharmacogenetics

Representative studies

Rare protein-altering variants in ANGPTL7 lower intraocular pressure and protect against glaucoma featured image

Rare protein-altering variants in ANGPTL7 lower intraocular pressure and protect against glaucoma

We identified an allelic series of rare protein-altering variants in ANGPTL7 that lower intraocular pressure and protect against glaucoma, highlighting ANGPTL7 as a therapeutic …

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Yosuke Tanigawa, Ph.D.
Genetics of 35 blood and urine biomarkers in the UK Biobank featured image

Genetics of 35 blood and urine biomarkers in the UK Biobank

We analyzed the genetic basis of 35 blood and urine biomarkers in UK Biobank. We revealed that genetic effects on biomarkers inform the genetic basis of disease.

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Yosuke Tanigawa, Ph.D.
Hypometric genetics: Improved power in genetic discovery by incorporating quality control flags featured image

Hypometric genetics: Improved power in genetic discovery by incorporating quality control flags

We introduce "hypometric genetics," an approach to investigate the genetic basis of binarized traits representing the presence of below-the-limit-of-quantification (BLQ) quality …

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Yosuke Tanigawa, Ph.D.